Crerar Trust has donated £10,000 to Reverse Rett to help fund research for a treatment or cure for Rett Syndrome - a neurological disorder effecting primarily girls.
The sole purpose of Reverse Rett is to speed treatments and a cure for Rett Syndrome and MECP2 related disorders, which totally devastate the lives of seemingly normal little children and their families.
Rett Syndrome is a neurological disorder effecting primarily girls. Most will develop normally for the first twelve or eighteen months of life, many even learning first words and taking their first steps. Then a regression occurs during which they loose their ability to speak and walk. It has been linked to developing the symptoms of autism, cerebral palsy, parkinson’s, epilepsy, and anxiety.
Reverse Rett is a parent-founded and parent-driven organisation. As the girls cannot speak for themselves it’s their parents and friends who join together in planning and implementing ways to raise funds for research. Crerar Trust’s donation will fun research to find either a profound treatment or a cure and a second reversal experiment in the US as part of a RSRT gene therapy programme.
The gene therapy research they are funding aims to find a new technique in delivering genes into the human body. The work of the scientists they want to support in Glasgow is adding invaluable knowledge to scientists around the world working in gene therapy for many different kinds of diseases. Their model for bringing scientists together is also a paradigm for how disease-focused organisations can facilitate collaboration and precipitate faster cures, helping the wider scientific community to deliver gene therapy treatment to countless others worldwide.